"Our aim is to make the lives of children better through advances in muscle and nerve research".

The problem. Neuromuscular disorders constitute one of the major causes of ongoing disability in childhood. While some of these disorders are treatable, for many children there is currently no cure.

Children with neuromuscular disorders have significant and worsening disabilities; many children are unable to walk and, in severe cases, the weakness impairs the muscles of breathing resulting in death at an early age.

Most neuromuscular disorders of childhood are genetic and more than one person in a family may be affected. For example, the muscular dystrophies are a group of hereditary muscle diseases, which can result in severe and often progressive muscle weakness. Inherited nerve disorders, known as peripheral neuropathies, can affect the transfer of messages within the body. When the muscle loses its nerve supply it "wastes away" resulting in progressive loss of motor function.

Scientific research aimed at solving clinical problems is the answer.