For over ten years the Institute for Neuroscience and Muscle Research has sought to answer fundamental questions about how our muscle, nerve and brain work when affected. Over this time our work touched the lives of many children and families, giving them hope for a happier and healthier future.
We now attract the best new researchers from Australia, New Zealand and Europe to lead the challenge to understand these disorders and develop therapies to make the lives of Australian children better.
A life without muscles is, sadly, often short and difficult. But our ground-breaking work is helping to change this. We now have therapies that slow down the development and progression of muscle weakness – so patients can walk and breathe independently for years longer. We are at the forefront of delivering novel therapies, such as targeted gene-based therapy and exon skipping to children with muscular dystrophy.
Our progress in developing and delivering therapies to children with neuromuscular disorders, has allowed us to investigate causes, consequences and treatments for other neurological conditions, such as neurofibromatosis, multiple sclerosis, childhood movement disorders and hydrocephalus.